A thousand thank yous... children win hope of CF wonder drug by autumn

A NEW generation of cystic fibrosis sufferers could be receiving a wonder drug by autumn.

- Chris Riches

Yesterday more than a thousand CF youngsters celebrated after its makers applied for approval for its use by six to 11-year-olds.

Since 2019 the Daily Express has fought for access to US firm Vertex’s incredible drug Kaftrio, hailed as “almost a cure for CF”.

Around 10,500 people in the UK have CF, a genetic illness that clogs the lungs with mucus and affects the pancreas, liver, kidneys and bowel. Only half of sufferers live to 32.

Last summer the NHS struck a deal for the wonder pill, meaning over 90 per cent of those aged 12 and over have access.

And now Vertex has finally applied to the UK drug regulator, the Medicines and Healthcare products Regulatory Agency, to give Kaftrio to the UK’s 1,300 suitable youngsters aged six to 11.

Vertex’s executive vice-president Nia Tatsis said: “Today’s news is an important milestone in broadening our access worldwide.”