Haemophilia is a serious bleeding disorder caused by a blood deficiency of clotting factors (factor VIII and factor IX proteins). It can lead to spontaneous bleeding episodes, joint damage, and a reduced quality of life for patients and their families.
The new gene therapy has shown promising results during the first phase trial on five patients, aged between 22 and 41. The annualised bleeding rate has been observed to be zero in all five patients over a cumulative follow-up of 81 months.
Denne historien er fra December 17, 2024-utgaven av The New Indian Express.
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Denne historien er fra December 17, 2024-utgaven av The New Indian Express.
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SOORI, AISHWARYA LEKSHMI TEAM UP FOR MAAMAN
PREVIOUSLY, we reported that actor Soori will be collaborating with Vilangu-fame director Prasanth Padiyaraj, for his next.
Suriya 45 adds Natty
ACTOR Natty, who was last seen in debutant Sidharth Vishwanath's Sorgavaasal, has joined hands with RJ Balaji once again in Suriya 45.
Aamir Khan's Sitaare Zameen Par wraps filming
The latest update from Aamir Khan's Sitaare Zameen Par, a spiritual sequel to the 2007 film Taare Zameen Par, is that the film's shoot has been wrapped and has entered the post-production stage.
THE UNTOLD STORY
Filmmaker Jayan Cherian speaks about his film Rhythm of Dammam, which explores the Siddi community in North Karnataka, and more
'Horror of this story is that it connects with today's world'
Director Magnus Von Horn and actor Vic Carmen Sonne discuss their recent film The Girl With The Needle, balancing social realism and commercial filmmaking, and more
Silent Hill 2 Remake: A little too foggy?
A little over three years ago, I finished my first ever horror title Resident Evil Village.
VROOM, VROOM
A LICENCE TO THRILL
Tales on the terrace
Stories, like old songs, have a way of resurfacing, finding new audiences and fresh contexts. On the evening of December 14, Chennai's Art on Terrace transformed into an intimate haven for such a tale, as author Renuka Narayanan breathed life into Mahadev, her 2019 book.
TIMELY REHAB KEY TO REGAIN FULL MOBILITY
ARVIND Sagar, 58, who had a history of hypertension and diabetes, suffered an ischemic stroke last July.
Gene therapy offers new hope to haemophilia patients
In a significant medical breakthrough, India's first human gene therapy with a lentiviral vector for severe haemophilia-A has been found to be successful with zero bleeding rate in patients.
